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Speakers

23rd Orphan Drugs and Rare Diseases Global Congress 2025 Europe

Innovative programmes to optimize access in a global healthcare market

Wednesday 19th - Thursday 20th March 2025

2024 KEY INDUSTRY EXPERT SPEAKERS

David Pearce

President of Innovation, Research, & World Clinic

Sanford Health

Anne-Sophie Chalandon

Head of Global Rare Diseases and CGT Policy

Sanofi

Pedro Franco

Director for Global Regulatory & Scientific Policy (GRASP)

Merck

Amanda Bok

Chief Strategy Officer

The Synergist

OWEN MARKS

Principal, OMGEN, Head of Rare Diseases and Diversity and Inclusion Co-Chair

Pfizer

Arti Patel

Genomics Associate, Great Ormond Street Hospital, Trustee

Treacher Collins

MANUELA MARONATI

Head of Rare Disease Europe

UCB

Alexander Natz

Secretary General

EUCOPE

RÜDIGER SCHULZE

VP & GM, Germany & Central/Eastern Europe

Ultragenyx

Nigel Nicholls

General Manager UK/Nordics & Baltics

Egetis Therapeutics AB

NICHOLAS BROOKE

Founder & Executive Director

Synergist

Julie Powell

Director, Patient Advocacy and Public Affairs

Pleco Therapeutics

KERRY LEESON-BEEVERS

Chief Executive

Alström Syndrome UK

Sheela Upadhyaya

Chair Elect, Rare Disease Special Interest Group

ISPOR

Dr. Femida Gwadry-Sridhar

Founder and CEO

Pulse infoframe Inc.

Nick Sireau

Chair & CEO

AKU Society

DR USMAN KHAN

Chair

Motor Neurone Disease (MND) Association

BOB STEVENS

Group CEO

MPS Society

MELANIE DIXON

Trustee

Cure DHDDS

DR. RON JORTNER

Founder/CEO

Aspire Biosciences

CAROLE SCRAFTON

Director & Co-Founder

Flutters and Strutters

ROHAN SIMON

Associate Director - Business Development

Insights Research Organization & Solutions

ANTHONY HALL

Chief Medical Officer

Healx

JOSHUA CARD-GOWERS

Senior Evidence Lead

HealthLumen

LINDSAY RANDALL

Founder, CEO, Mother

Arthur’s Quest

DR. HARRIET HOLME

Chair and Founder

PCDResearch.org

NICK SIREAU PHD

Chair and CEO

AKU Society

HAZEL DAWSON

Market Access Director UK & Ireland

Alexion Pharma UK

SURABHI VERMA

Chief Medical Officer

Leadiant Biosciences

JULIET HULSE

Head of Clinical Operations

Pulse infoframe Inc.

DAN LEWI

Head of Business Development and Patient Advocacy

Pulse infoframe Inc., Co- founder, CATS Foundation

ROBERT DONNELL

Executive Vice President – Medicines Access

Smartway Pharma

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