23rd Orphan Drugs and Rare Diseases Global Congress 2025 Europe
Innovative programmes to optimize access in a global healthcare market
Wednesday 19th - Thursday 20th March 2025
2024 KEY INDUSTRY EXPERT SPEAKERS
- Rüdiger Schulze, VP & GM, Germany & Central/Eastern Europe, Ultragenyx
- Nick Sireau, Chair & CEO, AKU Society
- Sheela Upadhyaya, Chair Elect, Rare Disease Special Interest Group, ISPOR
- David Pearce, President, Innovation & Research, Sanford Health
- Nigel Nicholls, General Manager UK/Nordics & Baltics, Egetis Therapeutics AB
- Alexander Natz, Secretary General, EUCOPE
- Anne-Sophie Chalandon, Head of Global Rare Diseases and CGT Policy, Sanofi
- Owen Marks, Head of Rare Diseases and Diversity and Inclusion Co-Chair, Pfizer
- Anthony Hall, Chief Medical Officer, Healx
- Arti Patel, Genomics Associate, Great Ormond Street Hospital, Trustee, Treacher Collins Family Support and Gene People UK
- Kerry Leeson-Beevers, Chief Executive, Alström Syndrome UK
- Amanda Bok, Chief Strategy Officer, The Synergist
- Nicholas Brooke, Founder & Executive Director, Synergist
- Bob Stevens, Group CEO, MPS Society
- Melanie Dixon, Trustee, Cure DHDDS
- Carole Scrafton, Director & Co-Founder, Flutters and Strutters
- Dr Usman Khan, Chair, Motor Neurone Disease (MND) Association
- Manuela Maronati, Head of Europe, Rare Disease Organization, UCB
- Rohan Simon, Associate Director - Business Development, Insights Research Organization & Solutions, an M42 Company
- Dr. Ron Jortner, Founder/CEO, Aspire Biosciences
- Joshua Card-Gowers, Senior Evidence Lead, HealthLumen
- Julie Powell, Director of Patient Advocacy and Public Affairs, Pleco Therapeutics
- Lindsay Randall, Founder, CEO, Mother, Arthur’s Quest
- Hazel Dawson, Market Access Director, UK & Ireland, Alexion Pharma
- Dr. Harriet Holme, Chair and Founder, PCDResearch.org
- Josie Godfrey, Director, JG Zebra Consulting, Joint CEO, Realise Advocacy
- Dr Peter Lanyon, Rare Diseases Clinical Lead, NHS England
- Pr Daniel Scherman, Head of Medicine, Life Sciences Division, European Academy of Sciences
- Dr. Femida Gwadry-Sridhar, Founder and CEO, Pulse infoframe Inc.
- Juliet Hulse, Head of Clinical Operations, Pulse infoframe Inc.
- Dan Lewi, Head of Business Development and Patient Advocacy , Pulse infoframe Inc., Co- founder, CATS Foundation
- Surabhi Verma, Chief Medical Officer, Leadiant Biosciences
David Pearce
President of Innovation, Research, & World Clinic
Anne-Sophie Chalandon
Head of Global Rare Diseases and CGT Policy
Pedro Franco
Director for Global Regulatory & Scientific Policy (GRASP)
Amanda Bok
Chief Strategy Officer
OWEN MARKS
Principal, OMGEN, Head of Rare Diseases and Diversity and Inclusion Co-Chair
Arti Patel
Genomics Associate, Great Ormond Street Hospital, Trustee
MANUELA MARONATI
Head of Rare Disease Europe
Alexander Natz
Secretary General
Nigel Nicholls
General Manager UK/Nordics & Baltics
NICHOLAS BROOKE
Founder & Executive Director
Julie Powell
Director, Patient Advocacy and Public Affairs
KERRY LEESON-BEEVERS
Chief Executive
Sheela Upadhyaya
Chair Elect, Rare Disease Special Interest Group
Dr. Femida Gwadry-Sridhar
Founder and CEO
Nick Sireau
Chair & CEO
DR USMAN KHAN
Chair
BOB STEVENS
Group CEO
MELANIE DIXON
Trustee
DR. RON JORTNER
Founder/CEO
CAROLE SCRAFTON
Director & Co-Founder
ROHAN SIMON
Associate Director - Business Development
ANTHONY HALL
Chief Medical Officer
JOSHUA CARD-GOWERS
Senior Evidence Lead
LINDSAY RANDALL
Founder, CEO, Mother
DR. HARRIET HOLME
Chair and Founder
HAZEL DAWSON
Market Access Director UK & Ireland
SURABHI VERMA
Chief Medical Officer
JULIET HULSE
Head of Clinical Operations
DAN LEWI
Head of Business Development and Patient Advocacy
Pulse infoframe Inc., Co- founder, CATS Foundation
DAN LEWI
Head of Business Development and Patient Advocacy
ROBERT DONNELL
Executive Vice President – Medicines Access