- 3rd - 4th April 2023
- Hilton London Kensington, London, United Kingdom
19th Orphan Drugs & Rare Diseases Global Congress 2023
Collaborations to Accelerate Rare Disease Drug Development and Access
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The Fastest Growing Orphan Drugs & Rare Diseases Networking Event.
Paradigm Global Events is again proud to present our Orphan Drugs and Rare Diseases Global Congress 2023 Europe. It’s the 19th in the series of our Flagship tri-annual Orphan Drugs & Rare Diseases event. This congress will provide you with a comprehensive
overview of the critical issues shaping the future of Orphan Drugs.
The COVID-19 Pandemic has impacted the lives of just about everyone, patients receiving
continuous treatment and care included. The Rare Disease community is already
experiencing considerable challenges in achieving early and detailed diagnosis and having
access to care and life-saving treatment, to chronic, highly complex, progressive, and
severely disabling nature of their diseases, which generate specific care needs. Undoubtedly,
during this crisis, the rare diseases community is experiencing unprecedented overall disruption even more…
According to a report by Fortune Business Insights, the Global Orphan Drugs Market size
will emerge from the COVID-19 crisis at a moderate growth during the forecast period of
2020 to 2026. The global orphan drugs market size is projected to reach USD 340.84 billion
by the end of 2027. As stated, the market was worth USD 151.00 billion in 2019 and will
exhibit a CAGR of 10.5% during the forecast period, 2020-2027.
The current regulatory climate increasing the number of regulatory approvals, expanding numbers of successful clinical trials related to these drugs, tremendous investments in R & D, and the interest and existence of several large-scale manufacturers, will create opportunities and contribute exponentially to the overall market growth.
The two-day Congress will provide an interactive, cutting edge, and comprehensive discussion and networking format led by key experts with intimate knowledge in the industry. Gain practical strategies and best practices on challenges, innovations, technologies, and concepts surrounding orphan drugs and rare diseases.
We look forward to meeting you at the Congress!
Sincerely yours,
Jocelyn Raguindin
Conference Director
Paradigm Global Events
GAIN LATEST INSIGHTS ON:
WHO SHOULD ATTEND?
This congress is specially created for valued stakeholders in the Rare Disease community:
Network with Presidents, Heads/Chiefs, VPs, Directors, and Managers in the area of:
President of Innovation, Research, & World Clinic
Chief Medical Officer, Gene Therapy and Inborn Errors of Metabolism
Director for Global Regulatory & Scientific Policy (GRASP)
CSO & General Manager
CEO
President and CEO
CEO
Chief Commercial Officer
Operations Lead
Senior Projects Officer
Founder & CEO
President EMEA
Content Rich Program Agenda! Featuring Keynote Presentations, Stream Sessions, Panel, and Round Table Discussions.
Kristin Smedley, CEO, Curing Retinal Blindness Foundation
Pedro Franco, Director for Global Regulatory & Scientific Policy (GRASP), Merck
Hannah Stark, Operations Lead, NIHR BioResource
Panelist:
Eric Crombez, Chief Medical Officer, Gene Therapy and Inborn Errors of Metabolism, Ultragenyx
Florence Barkats, Chief Commercial Officer, CISIV Ltd
Reserved
Manolo Bellotto, CSO & General Manager, Gain Therapeutics
Adrien Lemoine, Co-Founder & CEO, Bloomsbury Genetic Therapies
Panelist:
Hannah Stark, Operations Lead, NIHR BioResource
Panelist:
David Pearce, President of Innovation, Research & World Clinic, Sanford Health
David Pearce, President of Innovation, Research & World Clinic, Sanford Health
Sheela Upadhyaya, Chair Elect, Rare Disease Special Interest Group, ISPOR
Rüdiger Schulze, VP & GM, Germany & Central/Eastern Europe, Ultragenyx
Josie Godfrey, Co-Founder and CEO, Realise Advocacy
Panel Discussion:
Lara Bloom, President and CEO, The Ehlers-Danlos Society
Hannah Harvey, Senior Projects Officer, Beacon for Rare Diseases
Robert Mitchell-Thain, CEO, PBC Foundation
Nick Sireau, Chair & CEO, AKU Society
19th Orphan Drugs and Rare Diseases Global Congress 2023 Europe
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Take Advantage of the Super Early Bird Discount. Group Discounts Also Available.