9th Orphan Drugs and Rare Diseases Global Congress 2019 Europe
In the United States, a rare disease is defined as a condition affecting fewer than 200,000 people. In EU countries, any disease affecting fewer than 1 in 2,000 people is considered rare. That number may seem small, but it translates into approximately 246 000 people throughout the EU’s 28 member countries. Most patients suffer from even rarer diseases affecting 1 person in 100,000 or more.